Sanofi efdoralprin alfa earns orphan designation in EU for alpha-1 antitrypsin deficiency related emphysema
Paris: Sanofi has announced that the European Medicines Agency (EMA) has granted orphan designation to efdoralprin alfa (SAR447537, formerly known as INBRX-101), an investigational recombinant human alpha-1 antitrypsin (AAT)-Fc fusion…